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Porous Silicon Nanoneedles Efficiently Deliver Adenine Base Editor to Correct a Recurrent Pathogenic COL7A1 Variant in Recessive Dystrophic Epidermolysis Bullosa

by admin | Mar 12, 2025

Porous Silicon Nanoneedles Efficiently Deliver Adenine Base Editor to Correct a Recurrent Pathogenic COL7A1 Variant in Recessive Dystrophic Epidermolysis Bullosa

Mustfa, S. A., Dimitrievska, M., Wang, C., Gu, C., Sun, N., Romańczuk, K., Karpinski, P., Łaczmański, Ł., McGrath, J. A., Jacków‐Malinowska, J. & Chiappini, C., 12 Mar 2025, (E-pub ahead of print) In: ADVANCED MATERIALS.

Research output: Contribution to journal › Article › peer-review

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